Barbara Calhoun brings her vision of patient advocacy to to Indiana’s Rare Disease Advisory Council August 18, 2026
Beren Therapeutics Announces FDA Acceptance of its New Drug Application for Adrabetadex in Infantile-Onset Niemann Pick Disease Type C February 24, 2026
ND Expert Sean Kassen: Statement on first FDA-approved treatment for Niemann-Pick Type C disease September 23, 2024
